FDA Advisory Panel Recommends Sarepta’s Gene Therapy for Duchenne Muscular Dystrophy A pivotal step forward for Duchenne families as gene therapy shows promise to transform neuromuscular care. 12 months ago By John In Biopharma Highlights,FDA Approvals,Research Updates,Top Stories,
Vertex and CRISPR Therapeutics Secure First-Ever FDA Approval for CRISPR-Based Therapy in Sickle Cell Disease A historic breakthrough as the first CRISPR-based gene-editing therapy gains FDA approval, offering new hope for sickle cell … 12 months ago By John In Biopharma Highlights,FDA Approvals,Research Updates,Top Stories,