FDA Advisory Panel Recommends Sarepta’s Gene Therapy for Duchenne Muscular Dystrophy A pivotal step forward for Duchenne families as gene therapy shows promise to transform neuromuscular care. 1 year ago By John In Biopharma Highlights,FDA Approvals,Research Updates,Top Stories,
Vertex and CRISPR Therapeutics Secure First-Ever FDA Approval for CRISPR-Based Therapy in Sickle Cell Disease A historic breakthrough as the first CRISPR-based gene-editing therapy gains FDA approval, offering new hope for sickle cell … 1 year ago By John In Biopharma Highlights,FDA Approvals,Research Updates,Top Stories,